The European decision on Scholar Rock’s SMA treatment apitegromab will depend on upcoming FDA results from a U.S. plant ...

Serving as her friend Andrea's maid of honor enabled columnist Connie Chandler to reciprocate the kind of care Andrea always ...

After several excruciating months of hip pain, columnist Brianna Albers finally has not only an answer — arthritis — but a treatment plan.

England is expanding newborn screening to identify babies before SMA symptoms appear and support earlier treatment.

It's uncomfortable when people stare at her medical equipment, but columnist Alyssa Silva has learned to flip the script.

SMA patients with scoliosis show abnormal spinal muscle metabolism. These metabolic flaws lead to cellular energy deficiency ...

After 5 years on oral treatment Evrysdi, 90% of children with SMA type 1 were alive, and many reached motor milestones, a ...

The latest understandings in SMA disease type, severity, and progression. Plus, how to make an accurate diagnosis and ...

We are pleased to partner with the Muscular Dystrophy Association (MDA) to bring you coverage from the MDA Engage Symposium.

Alyssa Silva is a writer based out of Providence, Rhode Island. She was diagnosed with SMA type 1 in 1991 when she was just 5 months old. Aside from writing, Alyssa is the chief creative officer for ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google A former caregiver and friend once told me that she’d never spent ...

Itvisma, a one-time gene therapy for SMA, is now EU-approved for patients ages 2 and older. The expanded approval in Europe gives gene therapy access to older children, teens, and adults with SMA, ...