The European decision on Scholar Rock’s SMA treatment apitegromab will depend on upcoming FDA results from a U.S. plant ...

Serving as her friend Andrea's maid of honor enabled columnist Connie Chandler to reciprocate the kind of care Andrea always ...

After several excruciating months of hip pain, columnist Brianna Albers finally has not only an answer — arthritis — but a treatment plan.

England is expanding newborn screening to identify babies before SMA symptoms appear and support earlier treatment.

It's uncomfortable when people stare at her medical equipment, but columnist Alyssa Silva has learned to flip the script.

SMA patients with scoliosis show abnormal spinal muscle metabolism. These metabolic flaws lead to cellular energy deficiency ...

We are pleased to partner with the Muscular Dystrophy Association (MDA) to bring you coverage from the MDA Engage Symposium.

After 5 years on oral treatment Evrysdi, 90% of children with SMA type 1 were alive, and many reached motor milestones, a ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google Daily treatment with Evrysdi (risdiplam) may help stabilize or ...

When my great-aunt was 100, she used to sing a song that said “count your many blessings.” As I approach another birthday and complete another year on my journey with SMA, I’m counting my blessings ...

Muscle ultrasound effectively assesses muscle health in children with SMA. Children with SMA show muscle wasting and fat/connective tissue accumulation. Ultrasound links muscle structure to motor ...

One of the queerest ways to spend Pride Month could go like this … You decide to go to the theater one night. You scan the ticketing site for a show and land on one about lesbian identity, struggles, ...