Discover Sanfilippo Syndrome a rare genetic disorder affecting childrens development Learn about its symptoms treatment ...

It is a recessive X-linked disease, which means mothers have a 50 per cent chance of passing it to their sons. It is rare and ...

Equities researchers at Cantor Fitzgerald issued their FY2025 earnings per share estimates for Ultragenyx Pharmaceutical in a ...

Jupiter Neurosciences, Inc.’s JUNS share price has dipped by 59.50%, which has investors questioning if this is right time to ...

Stock analysts at Leerink Partnrs lifted their FY2024 EPS estimates for Ultragenyx Pharmaceutical in a report released on ...

Haliza Md Kasim’s eyes widened. Despite having gone through this before with her first son, Yusof, and despite the doctors ...

Nanosonics (ASX:NAN) has achieved a feather duster-to-rooster transformation with a bullish trading update for the December ...

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...

Israel’s Cease-Fires in Lebanon and Gaza Appear Fragile Israeli forces killed at least 15 people and injured dozens more in southern Lebanon on Sunday, Lebanese officials said. In Gaza, Israel ...

Jan. 24, 2025 — We're nearly one month into 2025, but if you're struggling to hold onto your New Year's resolution, stay strong, as new research shows that forming a healthy habit can take ...

Spinal cord compression (SCC) occurs in 5% to 30% of the oncology population and affects patient function, comfort, and general quality of life. Patients with lung cancer, breast cancer, prostate ...